Some great news from Bluebird Bio who is responsible for starting the clinical trial on gene therapy for ALD. They are currently recruiting boys affected by ALD to undergo treatment. Very exciting as this was first successful in France with Dr. Auborg and we have finally brought this to the United States. Gene Therapy is thought to be a safer method as there is no anti-rejection medications used since they are using the patients own cells.
Please see the link for more information.